Category Archives: Gene Therapy

In Vivo Gene Therapy for Cystic Fibrosis Part 3 In this video we discuss the use of In Vivo gene therapy to treat Cystic Fibrosis. By: Ben Garside … Continue reading →

In Vivo Gene Therapy for Cystic Fibrosis Part 1 In this video we discuss the use of In Vivo gene therapy to treat Cystic Fibrosis. By: Ben Garside … Continue reading →

Gene Therapy - "The Other Side" Original song by Gene Therapy. By: Aaron Bailey … Continue reading →

MPs will vote soon on a new gene therapy to stop incurable diseases passing to babies ending fears the Government is ducking the controversy. The health minister threw her weight behind a DNA-altering procedure pioneered by a team at Newcastle University, saying: This is something I want to take forward. Jane Ellison told a parliamentary inquiry: I am now actively seeking cross-Government approval for parliamentary time in this session to bring regulations before the House. Im extremely conscious that there are real families waiting on progress on this work. We need to keep up the momentum. The comments are a huge boost to the Newcastle team, which has called for legislation as soon as possible, because of the number of patients waiting for treatment. Also appearing before the Commons science select committee, the teams Professor Doug Turnbull said the worst-affected babies died within 24 or 48 hours. He said most diseases develop in childhood, or adolescence, adding: We can do a lot to help with epilepsy and diabetes, but there is no cure. And, on the gene therapy, This sort of approach to try to present a transmission of these sorts of diseases - would be really important. The treatment … Continue reading →

Gene Therapy - "Cumbersome" (7Mary3 cover) Rehearsal session with Gene Therapy. By: Aaron Bailey … Continue reading →

A new variation of gene therapy raises hopes for a safe and effective long-term treatment for X-linked severe combined immunodeficiency syndrome (SCID-X1), a life-threatening heritable disorder. The research was produced by a collaborative research team from Dana-Farber/Boston Children's Cancer and Blood Disorders Center, along with other institutions participating in an international clinical trial that involved boys from the United States and France. SCID-X1, dubbed bubble boy disease after a patient who lived for 12 years in a sterile bubble, is a rare genetic disorder that hinders the ability of individuals to combat infections. Because the disease is carried in an X-chromosome recessive pattern, the disorder occurs almost only in males. The resulting mutations inactivate a gene called IL-2 receptor gamma (IL2RG), severely weakening immune system functions. Left untreated, individuals who inherit the disorder usually die within a year. Previous gene therapy trials conducted in Europe over a decade ago promised dramatic progress, until a quarter of patients developed leukemia about two to five years following treatment. Scientists found that the previously used vectorthe device for transporting the correct gene in therapyinadvertently activated oncogenes, which can cause cancer. In this new study, the vector in use is a self-inactivating gammaretrovirus, which … Continue reading →

PUBLIC RELEASE DATE: 20-Oct-2014 Contact: Todd Murphy murphyt@ohsu.edu 503-494-8231 Oregon Health & Science University @ohsunews Oregon Health & Science University's Vaccine & Gene Therapy Institute (OHSU), has been awarded a $10 million contract from the National Institute of Allergy and Infectious Diseases (NIAID), part of the National Institutes of Health (NIH). Kineta, Inc., the University of Washington Center for Innate Immunity and Immune Disease (CIIID), and the Vaccine & Gene Therapy Institute of Florida (VGTI Florida) will collaborate with OHSU as major sub-contractors to develop new vaccine adjuvants that could boost the effectiveness of a wide range of human vaccines for infectious diseases including West Nile Virus, Dengue and Japanese Encephalitis. The work will also provide novel applications for enhancing the immune response against Ebola virus, HIV, and other virus infections. Infectious diseases affect millions of people in developed and developing nations, many with no effective protective vaccines. Vaccines are the first line of defense against infectious disease and have saved millions of lives over the years. However, some people with weakened immune systems and the elderly lose the ability to respond to vaccines. The effectiveness of vaccines can be improved by the addition of substances called adjuvants that not … Continue reading →

Living with Sanfilippo Syndrome: Reagan's Story Learn more about Gene Therapy: http://bit.ly/1vAhRiI Learn more about our clinical studies: http://bit.ly/1vAhOn7 Learn more about Dr. McCarty: http://bit.ly/1vAhODE Learn more about Dr. Flanigan:... By: NationwideChildrens … Continue reading →

Mining Gene Expression Data Focusing Cancer Therapeutics An understanding towards genetics and epigenetics is essential to cope up with the paradigm shift which is underway. Personalized medicine and gene therapy will confluence the days to come.... By: KAASHIV INFOTECH … Continue reading →

Gene Therapy Animation Video By: HotHoneyLips04 … Continue reading →