Category Archives: Muscular Dystrophy Treatment

The health ministry on Friday revealed a plan to attempt to decode the full genomes of around 90,000 cancer and other patients in about three years. Patients with deadly cancers will be the first subjects examined . The ministry hopes research on full genetic information, including DNA, will lead to discoveries on disease mechanisms, treatments and new drugs Continue reading →

Pratteln, Switzerland, November19, 2019 Santhera Pharmaceuticals (SIX: SANN) announces publication of the previously reported SYROS study data in prominent peer-reviewed medical journal Neuromuscular Disorders [1], demonstrating long-term efficacy with idebenone in slowing respiratory function loss in patients with Duchenne muscular dystrophy (DMD) under routine clinical care. Continue reading →

NS Pharma will share future plans for viltolarsen, its investigational exon-skipping therapy for Duchenne muscular dystrophy (DMD) in a webinar hosted byParent Project Muscular Dystrophy (PPMD) on Wednesday. The company will discuss viltolarsens mechanism of action and its current regulatory status during the one-hour webinar, which will be held Nov. Continue reading →

NEW HANOVER COUNTY, NC (WWAY) New Hanover County Fire Rescue is showing its continued support for the Muscular Dystrophy Association (MDA) as its members kick off the annual Fill the Boot fundraising campaign to raise money for those with muscular dystrophy. Continuing a 65-year tradition, dedicated firefighters from New Hanover County Fire Rescue will hit the streets with boots in hand asking pedestrians, motorists, and other passersby to make a donation to MDA on Thursday until Saturday from 8 a.m. 5 p.m Continue reading →

When I pray, I like to start by thanking God for all of the blessings he has bestowed on me. It reminds me of how much I have to be thankful for Continue reading →

18 November 2019 A gene therapytrial for Duchenne muscular dystrophy (DMD) has been halted after a patient experienced serious side effects. The clinical trial, run by the US life science company, Solid Biosciences, was put on hold by the FDA (Food and Drug Administration)after the patient had an adverse reaction in response to the experimental gene therapy, called SGT-001. Continue reading →

New York Jets long snapper Thomas Hennessy may only be in the league three years, but he is quite seasoned and polished. He spent time with the Indianapolis Colts before ultimately landing with the New York Jets. Continue reading →

I cant believe its been 13 years since I started exhibiting muscle loss. A lot has happened since then. My loss is slow but steady. Continue reading →

Photo Submitted A biomedical engineering faculty member has received a $50,000 award to pursue a new line of research into the immune systems role in genome engineering. Christopher Nelson, assistant professor of biomedical engineering, earned the funding through the American Society of Gene and Cell Therapys Career Development program. Continue reading →

Governor Proclaims World Duchenne Awareness Day in the State of Connecticut; Second state in the country to recognize this important day. In this season of thanks, Connecticut residents Christopher and Jessica Curran today expressed gratitude to both State Representative John Frey (R-111) and Governor Lamont for working together in a bipartisan fashion to raise awareness about their sons rare disease Duchenne Muscular Dystrophy. Continue reading →