Category Archives: Muscular Dystrophy Treatment

For many in Cheshire, The Spirit of Christmas at Chester Cathedral signals the start of the festive season. Now in its 24th year, this spectacular star-studded event has seen an array of popular television and film actors take to the stage to perform festive readings and songs. Continue reading →

Three new animal-model tests of a potential gene therapyfor oculopharyngeal muscular dystrophy (OPMD), known as BB-301, are planned, Benitec Biopharmaannounced. Results are expected tosupport a request for a Phase 1 clinical trial in patients. OPMD results from a faulty PABPN1 gene, leading to a protein that can form insoluble clumps linked with muscle weakness Continue reading →

NEW YORK, Oct. Continue reading →

A dad has shared his heartbreak at no longer being able to cuddle his daughters because of a muscle-wasting disease. Sam Hawyes, from Cwmbran, Wales, can barely even pick up a glass of water because of his type 2A limb-girdle muscular dystrophy condition. Mr Hawyes, 32, was diagnosed with the illness when he was 21 years old and it has become progressively worse over the years Continue reading →

This week, were looking at the enormous medical potential now being realised by gene therapy. Continue reading →

Gene therapy for HIV Ravi Gupta, Cambridge University; Michael Pepper, University of Pretoria Around the world, almost 40 million people are living with HIV. It grows in and progressively destroys the immune system, leaving victims highly susceptible to what would normally be trivial infections. Continue reading →

No one can accuse University of Missouri President Mun Choi of lacking bold aspirations or high expectations for the newly launched NextGen Precision Health Initiative. It is the most important and the largest project in the history of the UM system, he said recently on KCURs Up to Date. This is going to be a game-changer when it comes to developing life-saving treatments. Continue reading →

Global Muscular Dystrophy Treatment Market 2019 Research report provides information regarding market growth, cost structure, Keyplayers, revenue and forecast 2026. This report also includes the overall and comprehensive study of the Muscular Dystrophy Treatment market with all its aspects influencing the growth of the market. Continue reading →

Vertex Pharmaceuticals, the Boston drug maker best known for its cystic fibrosis treatments, continues to branch out, cutting a deal with a North Carolina-based biotech firm that is targeting several serious illnesses, including the fatal genetic disorder Huntingtons disease. In an agreement announced Monday, Vertex will pay Ribometrix $20 million up front to discover and develop at least two RNA-targeted medicines, with an option for a third. RNA or ribonucleic acid is a molecule found in all cells Continue reading →

A study has revealed that using DNA-like molecules to repair gene mutations in models could act as a successful therapy for patients. Continue reading →