Category Archives: Muscular Dystrophy Treatment

THE CANADIAN PRESS/FILE PHOTO An Air Canada plane landing at Pearson Airport. The P.E.I. Council of People with Disabilities is crying foul over the treatment of an Air Canada passenger with mobility issues after she was left stranded at the Montreal airport. The P.E.I. woman, who has muscular dystrophy, was not allowed to board her flight home to P.E.I. because a special chair Air Canada uses to disembark passengers with major mobility issues at the Charlottetown airport was out of order. Marcia Carroll, executive director of the P.E.I. Council of People with Disabilities, says the woman, who did not want to be identified, had to call her daughter in Toronto to come and pick her up in Montreal. I feel its negligible at the very least and criminal at the worst, Carroll said. She was left, at 11:30 at night, in the Montreal airport. Its horrible. If you didnt have family or that kind of support, what would you do? An official with Air Canada did confirm Monday the chair, known as a Washington chair, at the Charlottetown airport has been out of order for the last couple of weeks. The Washington chair is used to transport passengers who require … Continue reading →

Published on January 07, 2014 The P.E.I. Council of People with Disabilities is crying foul over the treatment of an Air Canada passenger with mobility issues after she was left stranded at the Montreal airport. Charlottetown Airport image from http://www.flypei.com The P.E.I. woman, who has muscular dystrophy, was not allowed to board her flight home to P.E.I. because a special chair Air Canada uses to disembark passengers with major mobility issues at the Charlottetown airport was out of order. Marcia Carroll, executive director of the P.E.I. Council of People with Disabilities, says the woman, who did not want to be identified, had to call her daughter in Toronto to come and pick her up in Montreal. I feel its negligible at the very least and criminal at the worst, Carroll said. She was left, at 11:30 at night, in the Montreal airport. Its horrible. If you didnt have family or that kind of support, what would you do? An official with Air Canada did confirm Monday the chair, known as a Washington chair, at the Charlottetown airport has been out of order for the last couple of weeks. The Washington chair is used to transport passengers who require the use … Continue reading →

Carli Carter crowd surfs at the Grand Kerfuffle last spring. Erin Burns/Daily Utah Chronicle file photo. I have plans, things I want to do, places I want to see, said Carter, a junior in broadcast journalism. She is actively involved on campus, holding the title of Brand Ambassador for Coca-Cola and Director of Archives for the Delta Gamma sorority. Im successful because I let myself be successful, Carter said. I wont allow being in a wheelchair to hold me back. Carter was in her first wheelchair when she was eight. At 14, she underwent a 12-hour-long surgery after the deterioration of her muscles left her with sclerosis and a collapsed lung. Ive torn both my meniscuses from my legs giving out on me, she said of moments she spends out of the chair. She dedicates time trying to inspire other community members who share her disease. In high school she was a state ambassador for the Muscular Dystrophy Association, with which she traveled all over Utah and Nevada talking about her story and encouraging others to live life to the fullest. Im tired of people thinking that because were in wheelchairs, we arent normal people, Carter said, I want to … Continue reading →

Sarepta Therapeutics (SRPT) shares cratered in November after the FDA told the company not to seek accelerated approval for its Duchenne muscular dystrophy drug eteplirsen. But what if FDA is changing its mind? FDA official Catherine Chew is sending a very interesting letter to people who write the agency in support of eteplirsen's early approval. I've reprinted the full text of the letter below, but check out this paragraph: Um... wow! Now, let's not get too excited. There has been no indication from Sarepta about a change in regulatory strategy, meaning the company is still focused on finalizing the design of the required eteplirsen phase III study. An agreement with FDA on that front is expected later this quarter. However, Chew's letter, suggests some wiggle room for the possibility that FDA would... might... possibly... be willing to review eteplirsen based on the existing phase II data. In fact, the same could be said for Prosensa (RNA) and GlaxoSmithKline's (GSK) drisapersen, if the companies decide to submit data from the failed phase III study. Sarepta shares are down 10% to $18.33 today because Citibank analyst Yaron Werber downgraded the stock to a sell. He doesn't believe eteplirsen has a chance in … Continue reading →

Drug May Partially Correct Deadly Form of Muscular Dystrophy By Daniel J. DeNoon WebMD Health News Reviewed By Louise Chang, MD Dec. 27, 2007 -- An "antisense" compound may partially correct the genetic defect that causes deadly Duchenne's muscular dystrophy. Researchers are not calling the finding a breakthrough, but they are cautiously optimistic that the approach may one day lead to a treatment that extends the lives of people afflicted with the always-fatal disease. Duchenne's muscular dystrophy is a genetic disease seen in one in 3,500 baby boys. The boy's muscles get weaker and weaker, landing them in wheelchairs by their twelfth birthday. Their hearts and lungs also weaken, and the brain may be affected. Most of these boys die in early childhood; with steroid treatment and breathing aids, their life span can be as long as 25 to 35 years. Nothing, however, prevents eventual death. Now there's a small glimmer of hope. Scientists now know the specific genetic mutation that causes Duchenne's muscular dystrophy. That mutation causes a "misreading" of the gene that encodes dystrophin, a substance crucial for muscle cell survival. In the test tube, a compound called an antisense oligonucleotide partially corrects this genetic misreading. It seems … Continue reading →

No two people with Duchenne or Becker muscular dystrophy (DBMD) are exactly alike. Therefore, the health issues will be different for each individual. Living a full life with DBMD may involve health care providers who know about different parts of the body all working together to address the needs of each individual. Most people who have Becker muscular dystrophy (BMD) receive treatments similar to those people who have Duchenne muscular dystrophy (DMD). It is important that a health professional be available to help coordinate care for anyone with muscular dystrophy. Depending on local services, any one of a wide range of health care professionals can serve as a coordinator of clinical care. These health care professionals can include: The care coordinator should understand muscular dystrophy and the treatments that are needed. Care for DMD includes monitoring muscle health. Muscle weakness happens in BMD as well, but usually at a slower rate. People who have DMD experience progressive muscle weakness because they do not have enough dystrophin (a protein) to help keep the muscles strong and healthy. Although every person is different, the muscle weakness in DMD often follows a certain path. The problems caused by muscle weakness can include difficulty … Continue reading →

EAST PALESTINE, Ohio (WKBN) - A top 40 recording artist from East Palestine is turning her focus from music to finding a cure for Muscular Dystrophy. Sarah Burgess is a former American Idol contestant. Her brother has Duchenne Muscular Dystrophy, as does her friend Billy Ellsworth. For the first time, there's real hope for a treatment that can help. A clinical trial for a new drug is showing significant progress for boys with the disease. But first, it has to be approved by the FDA. "Please let us decide. Let the families decide if this is right for their child," Burgess said. Her friend, Billy Ellsworth, 12, is part of the trial. "It doesn't make you walk as good. It makes your legs hurt a lot," Billy said But the new drug has changed everything. "It's helped me a lot. It's made me walk for a long time," Billy said. "Billy, he's getting so much stronger. He can do so many amazing things. He's such an amazing kid. And then it's really hard to see my brother," Burgess said. That's why Burgess, Billy and Billy's mom Terri are working hard to get the drug that's helping Billy approved by the … Continue reading →

Deepak Arora DMD Post Treatment - Part 1 stem cell india, stem cell therapy india, stem cell in india, stem cell therapy in india, india stem cell, india stem cell therapy, duchenne muscular dystrophy india, duchenne muscular dystrophy... By: Stem Cell India … Continue reading →

Deepak Arora DMD Post Treatment - Part 3 stem cell india, stem cell therapy india, stem cell in india, stem cell therapy in india, india stem cell, india stem cell therapy, duchenne muscular dystrophy india, duchenne muscular dystrophy... By: Stem Cell India … Continue reading →

Deepak Arora DMD Post Treatment - Part 2 stem cell india, stem cell therapy india, stem cell in india, stem cell therapy in india, india stem cell, india stem cell therapy, duchenne muscular dystrophy india, duchenne muscular dystrophy... By: Stem Cell India … Continue reading →