There has been much excitement over the announcements of results of the Gene Therapy trials conducted by Dr Robin Ali (fast becoming a hero in my world!). The trial is for a treatment for LCA, Leber's Congenital Amaurosis, a rare form of a Retinal Disease / Retinitis Pigmentosa and has produced some amazing results. This video shows the before and after results of Steven navigating a darkened room with obstacles in his way.
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First results of Gene Therapy Trials by Professor Robin Ali
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